#rare diseases

Collection of rare diseases news, found 34 news.

Aptorum Group announces significant progress of repurposed drug candidate, SACT-1 for neuroblastoma targeting IND submission in H2 2020

- Aptorum Group Limited (Nasdaq: APM) (“Aptorum Group”), a biopharmaceutical company focused on the development of ...

Invicro LLC announces Dr. Matthew Silva as new Chief Executive Officer and Dr. Jack Hoppin is named President of Konica Minolta Precision Medicine

- Invicro LLC, a Konica Minolta company, today announces, Dr. Matthew Silva has been appointed as the new Chief ...

Takeda continues strategic divestitures with sale of select OTC and non-core assets to STADA for $660 million USD

- Takeda Pharmaceutical Company Limited (TSE:4502/NYSE:TAK) (“Takeda”) today announced that it has entered into an ...

Takeda agrees to divest select OTC and non-core assets to Acino for over $200 million USD

- Takeda Pharmaceutical Company Limited (TSE:4502/NYSE:TAK) (“Takeda”) today announced that it has entered into an ...

Takeda completes sale of Xiidra® to Novartis

- Takeda Pharmaceutical Company Limited (TSE:4502/NYSE:TAK) (“Takeda”) today announced the completion of its sale ...

Takeda simplifies portfolio and accelerates deleveraging through two divestitures

- Takeda Pharmaceutical Company Limited (TSE:4502/NYSE:TAK) (“Takeda”) today announced that it has entered into ...

Four rare diseases found in Indonesia

Of the 8000 rare disease in the world, at least four were found in Indonesia, namely Mukopolisakaridosis (MPS) type II, ...

Celgene and Acceleron announce luspatercept achieved primary and all key secondary endpoints in phase III 'BELIEVE' study in adults with transfusion-dependent beta-thalassemia

- Celgene Corporation (NASDAQ: CELG) and Acceleron Pharma Inc. (NASDAQ: XLRN) today announced results from a phase III, ...

Denis DELVAL is appointed CEO of LFB SA

- On December 20th, a decree from the President of France was published in Le Journal Officiel* appointing Denis DELVAL ...

PMC Group International announces acquisition of pharma company in France

- PMC Group France, a wholly owned subsidiary of PMC Group International Inc., which is an independent arm of PMC Group ...

Impact of Early Insulin Initiation on Glycemic Control in Asian People with Type 2 Diabetes

-     Two studies presented at World Diabetes Congress 2011 provide further evidence of the ...

Investigational Oral Multiple Sclerosis Therapy Teriflunomide (*) Aubagio (R)) Significantly Reduced

-            - Findings from Two-Year Pivotal Phase III TEMSO Trial ...

More Patients with Type 2 Diabetes Reach HbA[1c] Target with Apidra(R) on top of Lantus(R)

-            - First Randomized Controlled Trial to Show That Basal Plus ...

Sanofi Announces Nursing Recognition Program to Help Turn Caring Ideas Into Reality

--- Nurses Worldwide are Encouraged to Enter an Exciting Recognition Program Which Showcases Their Creativity and Their ...